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全球获批的小核酸药物共计23款
全球获批的小核酸药物共计23款
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所属报告:
siRNA药物行业深度报告:小核酸大时代靶向治疗新纪元-251014(23页).pdf
打包全文图表
相关数据
图27:iPhone17Pro(256GB)和iPhone7的价格(来自2017年《世界价格地图》版本,完整可用列表,美元)
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行业数据
2026-07-21
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地图来源:自然资源部标准地图服务系统-世界地图,审图号:GS(2016)2945号
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2026-07-13
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图8-8:国际武术联合会 《第五届世界太极拳锦标赛竞赛规程》,2026年4月23一30日
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行业数据
2026-07-01
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2000~2025年世界一次能源费结构
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行业数据
2026-07-01
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中国化工产品销售规模占比世界46%(2024年)
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市场规模
2026-07-01
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世界主要运载火箭发射报价(万美元)和运载能力(kg)对比
fCDlnLDljLogfCDngavnrq0gfCDljZXmrKHmiqXku7fvvIjkuIfnvo7lhYPvvIkgfCDovb3ojbfog73lipvkuIrpmZDvvIhMRU/ov5DlipvvvJtrZ++8iSB8IOWNleWFrOaWpOaKpeS7t++8iOS4h+e+juWFgy9rZ++8iSB8CnwgLS0tLSB8IC0tLS0gfCAtLS0tIHwgLS0tLSB8IC0tLS0gfAp8IOe+juWbvSB8IOeMjum5sDnlj7cgfCA3NDAwIHwg57qmMjIwMDAgfCAwLjI3IHwKfCDnvo7lm70gfCDph43lnovnjI7pubAgfCA5NzAwIHwg57qmNjM4MDAgfCAwLjE0IHwKfCDmrKfmtLIgfCDpmL/kuL3kuprlqJw25Y+377yI5Y+M5Yqp5o6o6YWN572u77yJIHwgODgwMCB8IDEwMDAwLTE1MDAwIHwgMC43MCB8Cnwg5qyn5rSyIHwg6Zi/5Li95Lqa5aicNuWPt++8iOWbm+WKqeaOqOmFjee9ru+8iSB8IDEwNjAwLTEyMDAwIHwgMjAwMDArIHwgMC42MCB8Cnwg5qyn5rSyIHwg57uH5aWz5pifIHwgMzcwMCB8IDIzMDAgfCAxLjYxIHwKfCDkv4TnvZfmlq8gfCDogZTnm58y5Y+3IHwgMzUwMCB8IDcwMDAtODUwMCB8IDAuNTAgfAp8IOS/hOe9l+aWryB8IOi0qOWtkE0gfCA2NTAwIHwgNjAwMCB8IDEuMDggfAp8IOS4reWbvSB8IOmVv+W+gTPlj7cgfCAyMDAwIHwgNzUwMC04MDAwIHwgMC4yNSB8CgrmnaXmupDvvJpOZXh0IFNwYWNlZmxpZ2h0LCBSdXNzaWFuIFNwYWNlIFdlYiwg5Lit5rOw6K+B5Yi456CU56m25omA
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行业数据
2026-06-26
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2026年中国球迷观看往届世界杯时长
fCDop4LnnIvlvoDlsYrkuJbnlYzmna/ml7bplb8gICAgICAgfCDljaDmr5QgICB8CnwtLS0tLS0tLS0tLS0tLS0tLS0tLS0tLS0tLXwtLS0tLS0tLXwKfCDkuI3liLAx5bGK77yI5LuK5bm05Yia5byA5aeL5YWz5rOo77yJIHwgNS43JSAgIHwKfCAxIC0gM+Wxiu+8iDQgLSAxMuW5tO+8iSAgICAgIHwgNTQuOCUgIHwKfCA0IC0gNuWxiu+8iDEzIC0gMjTlubTvvIkgICAgIHwgMzIuNyUgIHwKfCA35bGK5Lul5LiK77yIMjXlubTku6XkuIrvvIkgICAgICB8IDYuOCUgICB8CgrotYTmlpnmnaXmupDvvJoyMDI25bm05Lit5Zu955CD6L+36KeC55yL5b6A5bGK5LiW55WM5p2v5pe26ZW/55u45YWz5Zu+6KGo
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行业数据
2026-06-15
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截至2026年5月4日,美国海军在世界各地部署的航母打击群和两栖戒备群的大致位置
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行业数据
2026-06-12
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中国港口吞吐量世界排名领先,全球TOP10
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行业数据
2026-06-12
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中国港口吞吐量世界排名领先,全球TOP10货
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行业数据
2026-06-12
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图3-1丨世界能源可持续性总分(2022)
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行业数据
2026-06-09
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世界各国家(140个)
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2026-06-09
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2025世界能源可持续性评价报告|聚焦全球性冲击影响
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2026-06-09
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世界半导体贸易规模及半导体行业指数均明显上行
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市场规模
2026-06-09
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印尼——政府发展绿能意愿强烈,但作为产油国,电气化转型内生动力不足(图为世界主要国家油价排序)
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2026-06-02
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2026-07-30
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行业数据
2026-07-30
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小核酸药物具有较强的靶点拓展能力,在罕见病领域率先验证平台价值。截至目前,全球已获批的小核酸药物共计 23 款,其中 siRNA 药物 7 款,ASO 药物 14 款(其中 2 款已退市)、Aptamer 药物 2 款(其中 1 款已退市)。从企业端来看,siRNA 获批药物中,大部分由 Alnylam 开发或者参与开发,而 ASO 药物产品获批较多的企业为 Ionis 和 Sarepta。从适应症来看,小核酸药物在罕见病上率先突破,已经获批上市的小核酸药物针对的罕见病有11 种,涉及 19 个产品,我们认为主要的原因包括:1)罕见病可以利用孤儿药政策快速获批,且通过高定价迅速回收成本,以便后续推进其他更大的疾病领域的开发;2)小核酸药物可通过二维的 mRNA 与 Watson-Crick碱基配对,理论上只需要选择沿靶向 mRNA 的正确核苷酸序列,有靶向现有治疗方式中“无法成药”的靶点的潜力。
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siRNA药物行业深度报告:小核酸大时代靶向治疗新纪元-251014(23页).pdf
2026年siRNA药物行业报告:技术平台成熟,常见病拓展开启靶向治疗新纪元
siRNA药物行业深度报告:小核酸大时代靶向治疗新纪元-251014
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